Tag Archive: rare pediatric voucher


Pitching a rare disease treatment, vouchers and more underscores need for collaboration

Over the last few weeks I have been pitching the Phoenix Nest enzyme replacement work with LaBioMed in New York, working on proofs for several papers (here and here) and putting a blog together on the need for the rare pediatric disease priority review voucher. This is in addition to the usual grant writing projects …

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